Document Type

Article

Publication Date

2-4-2019

Identifier

DOI: 10.1038/s41598-018-37940-6; PMCID: PMC6362041

Abstract

Acetaminophen (APAP) is a commonly used analgesic responsible for more than half of acute liver failure cases. Identification of previously unknown genetic risk factors would provide mechanistic insights and novel therapeutic targets for APAP-induced liver injury. This study used a genome-wide CRISPR-Cas9 screen to evaluate genes that are protective against, or cause susceptibility to, APAP-induced liver injury. HuH7 human hepatocellular carcinoma cells containing CRISPR-Cas9 gene knockouts were treated with 15 mM APAP for 30 minutes to 4 days. A gene expression profile was developed based on the 1) top screening hits, 2) overlap of expression data from APAP overdose studies, and 3) predicted affected biological pathways. We further demonstrated the implementation of intermediate time points for the identification of early and late response genes. This study illustrated the power of a genome-wide CRISPR-Cas9 screen to systematically identify novel genes involved in APAP-induced hepatotoxicity and to provide potential targets to develop novel therapeutic modalities.

Journal Title

Sci Rep

Volume

9

Issue

1

First Page

1396

Last Page

1396

MeSH Keywords

Acetaminophen; Animals; CRISPR-Associated Protein 9; CRISPR-Cas Systems; Cell Line, Tumor; Databases as Topic; Gene Expression Regulation; Genes, Regulator; HEK293 Cells; Hepatocytes; Humans; Male; Mice, Inbred C57BL; Reproducibility of Results; Signal Transduction

Keywords

Acetaminophen; Animals; CRISPR-Associated Protein 9; CRISPR-Cas Systems; Cell Line, Tumor; Databases as Topic; Gene Expression Regulation; Genes, Regulator; HEK293 Cells; Hepatocytes; Humans; Male; Mice, Inbred C57BL; Reproducibility of Results; Signal Transduction

Comments

This article is licensed under a Creative Commons Attribution 4.0 International License, which permits use, sharing, adaptation, distribution and reproduction in any medium or format, as long as you give appropriate credit to the original author(s) and the source, provide a link to the Creative Commons license, and indicate if changes were made. The images or other third party material in this article are included in the article’s Creative Commons license, unless indicated otherwise in a credit line to the material. If material is not included in the article’s Creative Commons license and your intended use is not permitted by statutory regulation or exceeds the permitted use, you will need to obtain permission directly from the copyright holder. To view a copy of this license, visit http://creativecommons.org/licenses/by/4.0/.

Publisher's Link: https://www.nature.com/articles/s41598-018-37940-6

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